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Stanford researchers have uncovered how a genetic mutation contributes to a heart disease known as familial dilated cardiomyopathy. Existing drugs correct the defect in heart cells grown in a petri dish, suggesting a new therapeutic target.

In preclinical trials, Stanford scientists and their collaborators harnessed the gene-editing system CRISPR-Cas9 to replace the mutated gene underpinning the devastating immune disease.

Mary Leonard, chair of the Department of Pediatrics at Stanford, works to understand exactly how chronic diseases hurt children’s bone health.

A Stanford-led national collaboration to procure and analyze human pancreatic tissue from deceased donors illustrates how the organ’s function changes as we age, and could point the way toward new diabetes treatments.