Stanford Autonomic Disorders Program Clinical Trials

North American Prodromal Synucleinopathy Stage 2 (NAPS2) Consortium
PI: Mitchell Miglis, MD
Study Status: Closed to enrollment
Research Coordinator: Adele Viviani
Contact: autonomicresearch@stanford.edu

Open-label prospective study for immune therapies in autoimmune gastrointestinal dysmotility (AGID)
PI: Dong-In Sinn, MD
Study Status: Open to enrollment
Research Coordinator: Barbara Hung
Contact:  autonomicresearch@stanford.edu

Syn-Sleep Study
PI: Mitchell Miglis, MD
Study Status: Closed to enrollment
Research Coordinator: Adele Viviani
Contact: autonomicresearch@stanford.edu

A Phase 2, double-blind, placebo-controlled, parallel-group study to assess the safety, tolerability, pharmacokinetics, pharmacodynamics, and potential efficacy of multiple doses of ONO-2808 in patients with Multiple System Atrophy (MSA)
PI: Mitchell Miglis, MD
Study Status: Closed to enrollment
Research Coordinator: Jordan Seliger or Barbara Hung
Contact: autonomicresearch@stanford.edu

A Phase 2 Double-Blind Placebo-Controlled Single-Dose Study of Pharmacodynamics, Pharmacokinetics, Safety, and Tolerability of REGN7544, an NPR1 Antagonist Monoclonal Antibody, in Patients with Postural Orthostatic Tachycardia Syndrome
PI: Mitchell Miglis, MD
Study Status: Open to enrollment
Research Coordinator: Barbara Hung
Contact: autonomicresearch@stanford.edu

A Phase 3, Randomized, Multicenter, Double-Blind, PlaceboControlled Study of Acoramidis for Transthyretin Amyloidosis Prevention in the Young (ACT-EARLY Trial)
PI: Safwan Jaradeh, MD (Cardiovascular Medicine PI: Kevin Alexander, MD)
Study Status: Open to enrollment
Research Coordinator: Adele Viviani
Contact: autonomicresearch@stanford.edu

Effect of low sodium oxybate (LXB) on autonomic symptom burden in idiopathic hypersomnia patients with postural tachycardia syndrome: a placebo-controlled, double-blind, randomized withdrawal study
PI: Mitchell Miglis, MD
Study Status: Enrolling soon
Research Coordinator: Jordan Seliger or Barbara Hung
Contact: autonomicresearch@stanford.edu

Ultrasound Guided Stellate Ganglion Block in Postural Tachycardia Syndrome: A randomized double blind sham placebo-controlled pilot study
PI: Mitchell Miglis, MD (Anesthesia PI: Anna Maria Bombardieri, MD, PhD)
Study Status: Open to enrollment
Research Coordinator: Barbara Hung
Contact: autonomicresearch@stanford.edu