Event Recordings
Day 1 | Day 2
Session VI: Academia to Industry and Back
Moderators: Yevgeniya Nusinovich, MD, PhD (Senior Editor, Science) and Sanjay Malhotra, PhD (Professor, Oregon Health & Science University)
Session IV Full Recording
Designer DNA Drug Therapy for Neurodegenerative Disease
Don Cleveland, PhD
Department Chair, Cellular and Molecular Medicine (CMM); Professor, Cellular and Molecular Medicine, University of California San Diego
Toward Universal Druggability
Gregory Verdine, PhD
Erving Professor of Chemistry, Harvard University
Drug Discovery at Fred Hutch Cancer Center
Thomas Lynch, MD
President and Director, Fred Hutchinson Cancer Center
Session VI Panel Discussion
Session VIII: Drug Discovery II: Core Principles and Frontiers
Moderators: Fady Malik, MD, PhD (Executive Vice President of Research and Development, Cytokinetics) and Mark Mercola, PhD (Professor, Stanford University School of Medicine)
Session VIII Full Recording
Discovery of an Orally Bioavailable Macrocyclic PCSK9 Inhibitor
George Addona, PhD
Senior Vice President and Head, Discovery, Preclinical Development, and Translational Medicine, Merck Research Laboratories
Data & Patients: Novel Partners in Drug Development
Paul Burton, MD, PhD
Senior Vice President and Chief Medical Officer, Amgen
Plaiting The Golden Braid: Incorporating Patient-Generated Data In Clinical Development
Andrew Trister, MD, PhD
Chief Medical Officer and Chief Scientific Officer, Verily Life Sciences
Future Advances in the Treatment of Neuromuscular Disorders
Paulo Fontoura, MD, PhD
Global Head and Senior Vice President of Neuroscience, Immunology, Ophthalmology, and Rare Diseases, Roche
Session VIII Panel Discussion
Session IX: Perspectives and Opportunities in Translational Research and Therapeutics
Moderators: Carolyn Bertozzi, PhD (Baker Family Director of Stanford ChEM-H, Anne T. and Robert M. Bass Professor, Stanford University), and Kuldev Singh, MD (Professor, Stanford University School of Medicine)
Session IX Full Recording
Delivering on the Promise of Genetic Medicines
Peter Marks, MD, PhD
Director, Center for Biologics Evaluation and Research, Food and Drug Administration
Advances and Innovations in CDER’s Approach to Drug Development
Patrizia Cavazzoni, MD
Director, Center for Drug Evaluation and Research, Food and Drug Administration
Update on CIRM Funding Programs
Rosa Canet-Avilés, PhD
Vice President, Scientific Programs & Education, California Institute for Regenerative Medicine
Translational Science: Maximizing the Success of Therapeutic Development
Joni Rutter, PhD
Director, National Center for Advancing Translational Sciences, National Institutes of Health
AI and Drug Discovery @ ARPA-H
Wade Shen
Director of Proactive Health Office, Advanced Research Projects Agency for Health (ARPA-H)