2020
Tuesday Tue
4th Annual CDCM Symposium
REGISTER NOW!
The CDCM is a joint initiative of the Stanford University School of Medicine, Stanford Health Care and Stanford Children’s Health. The Center provides the organizational and physical infrastructure to support investigator-initiated clinical translational studies on stem cell and gene therapy from initial discovery through completion of clinical proof-of-concept studies.
This scientific conference will bring together clinicians, basic scientists, patient advocates, translational investigators and experts from the biotech/pharmaceutical field to discuss the process of how discoveries in gene and cell therapy are translated to clinical trials and ultimately commercialized.
PROGRAM
7:30-8:00am |
Breakfast |
8:00-8:15am |
Opening Remarks |
8:15-8:20am |
Welcome: Maria Grazia Roncarolo, MD, Director, CDCM, Stanford University |
Opening Keynote |
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8:20-9:10am
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Introduction of Keynote: Matthew Porteus, MD, PhD, Co-Director, CDCM, Stanford University Keynote: Luigi Naldini, MD, PhD, Director, San Raffaele Telethon Institute for Gene Therapy Title: “Advanced Hematopoietic Stem Cell Gene Therapy for Genetic Diseases and Cancer” |
Session 1: New Cell-Based Medicine Discoveries
Moderator: Fraser Wright, PhD, Professor of Pediatrics, CDCM
9:10-9:35am |
Philip Beachy, PhD, The Ernest and Amelia Gallo Professor in the School of Medicine, Professor of Urology, of Developmental Biology and, by courtesy, of Chemical and Systems Biology, Stanford University Title: “Why do We Need Stem Cell Replacement Therapy for Definitive Treatment of Bladder Cancer?” |
9:35-10:00am |
Charles Kwok Fai Chan, PhD, Assistant Professor of Surgery (Plastic & Reconstructive Surgery), Stanford University Title: “Understanding and Engineering Skeletal Stem Cell Niches” |
Regulation of Cell and Gene Therapy |
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10:00-10:30am |
Introduction: Bruce Burnett, PhD, Interim Executive Director, LCGM, Stanford University Elizabeth Hart, MD, Office of Tissues and Advanced Therapies, CBER, FDA Title: “Cell and Gene Therapy: A Regulatory Perspective” |
10:30-11:00am |
BREAK |
Session 2: Pre-Clinical Development of Curative Medicines
Moderator: Mary Leonard, M.D., M.S.C.E.
11:00-11:25am |
Anthony Oro, MD, PhD, Co-Director, CDCM, Stanford University Title: “Uses of a Chromatin Dynamic Map for Manufacturing CRISPR-corrected IPS-derived Skin Grafts” |
11:25-11:50am |
Bertha Chen, MD, Professor of Obstetrics and Gynecology (Gynecology - Urogynecology) and, by courtesy, of Urology at the Stanford University Medical Center Title: “Stem Cell-Derived Therapy for Soft Tissue Regeneration” |
Models of Academic/Private Collaboration |
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11:50-12:30pm |
Introduction: Devan Shah, Director of Business Development, CDCM, Stanford University Steven M. Altschuler, MD, Managing Director, Healthcare Ventures, at Ziff Capital Partners Title: “Spark Therapeutics: A New Model for Commercializing Academic IP and Partnering with Industry and Investors” |
12:30-1:30pm |
LUNCH |
Session 3: Clinical Trials in Curative Medicines
Moderator: Natalia Gomez-Ospina, MD, PhD
1:30-1:55pm |
Thomas Rando, MD, PhD, Professor, Neurology & Neurological Sciences, Stanford University Title: “Muscle Stem Cells: Molecular Regulation and Translational Potential” |
1:55-2:20pm |
Kara Lynn Davis, DO, Assistant Professor, Hematology/Oncology, Stanford University Title: “CAR-T cells for Leukemia: Insights into Successes and Failures” |
Manufacturing of Cell and Gene Therapies |
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2:20-3:00pm |
Introduction: Irv Weissman, MD, Director, Institute of Stem Cell Biology and Regenerative Medicine, Stanford University Stefan Miltenyi, President, Miltenyi Biotec Inc. Title: “Making Cell and Gene Therapies Available to Many Patients” |
3:00-3:30pm |
BREAK |
Physician Advocacy for Patients
3:30-4:00pm |
Introduction: Matthew Porteus, MD, PhD, Co-Director, CDCM, Stanford Wanda Whitten-Shurney, MD, CEO and Medical Director, Sickle Cell Disease Association of America (SCDAA) Title: “Sickle Cell Disease Up Close and Personal” |
Closing Keynote: |
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4:00-4:45pm |
Introduction of Keynote: Anthony Oro, MD, PhD, Co-Director, CDCM, Stanford Keynote: Gordon Keller, PhD, Director of the McEwen Stem Cell Institute, University Health Network, Toronto Canada Title: “Translating Human Development to New Therapies” |
4:45-4:50pm |
Closing Remarks: Maria Grazia Roncarolo, MD, Director, CDCM, Stanford University |
5:00-6:00pm |
WINE & CHEESE RECEPTION |
EVENT SPONSORS
Maternal & Child Health Research Institute
Panacea Venture
Synthego
Abeona Therapeutics
Aldevron
