March 15 Mar 15
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Event Sponsors


CDCM 7th Annual Symposium

Registration is now open!

Join us for the CDCM's 7th annual symposium and learn about new cell, gene, and regenerative medicine discoveries, pre-clinical development and clinical trials of curative medicines, and challenges with bringing these cures to patients to meet unmet medical needs. Exploration and discussion of these topics will be held at this one-day conference for clinicians, basic scientists, patient advocates, translational investigators, and biotech and pharmaceutical experts. More than 700 people are expected to attend, including a growing number of international participants from Europe, Asia Pacific, and the Middle East. This year, we are offering virtual participation as well as a return to in-person attendance!

The symposium is now over. Thank you all to those who attended!

Platinum Sponsor

Each year, the CDCM hosts an annual symposium to engage in scientific discussion about new discoveries and developments in the cell and gene therapy field. The 7th annual symposium will host speakers to present on topics related to the field, including new cell, gene, and regenerative medicine discoveries; pre-clinical development and clinical trials of curative medicines; and challenges with bringing these cures to patients with unmet medical needs.

Hans Clevers, PhD will be the keynote speaker and present on his work in organoids and pre-clinical models to accelerate IND enabling studies. In addition, we will be hosting the director of the Center for Biologics Evaluation and Research (CBER) at the FDA, Peter Marks, MD, PhD

Additionally, this year's symposium seeks to highlight 2 products that were developed by the CDCM and tell the story from the bench to bedside. Alongside this year's host of renowned speakers, the stories of the gene-corrected sickle cell and epidermolysis bullosa tissue correction products will be extensively discussed.

Gene-Corrected Sickle Cell:

  • Matthew Porteus, MD, PhD
  • David Shyr, MD
  • Jerry Cacia, CTO, Graphite Bio
  • Zariah Stevenson, SCD Patient Perspective


Epidermolysis Bullosa Tissue Correction:

  • Anthony Oro, MD, PhD
  • Jean Tang, MD, PhD
  • Michael Hund, MBA
  • Charlotte Brown, EB Patient Perspective

Projected Schedule

Opening Remarks
8:00 - 8:30 AM Lloyd Minor, MD, Dean, School of Medicine, Stanford University
Paul King, President and CEO, Stanford Children's Health
David Entwistle, President and CEO, Stanford Healthcare
Matthew Porteus, MD, PhD, Diretor, CDCM, Stanford University
Opening Keynote (Virtual)
8:30 - 9:10 AM

Keynote Speaker: Hans Clevers, MSc, MD, PhD, Head of Pharma Research and Early Development, Roche, Basel Switzerland

"Organoids to Model Human Disease"

Epidermolysis Bullosa Tissue Correction Therapy Panel

Moderator: Rosa Bacchetta

9:15 - 10:30 AM Anthony Oro, MD, PhD, Associate Director, CDCM, Stanford University
Jean Tang, MD, PhD, Professor of Dermatology, Stanford University
Michael Hund, MBA, CEO, EB Research Partnership
Charlotte Brown (Patient Perspective)
10:30 - 11:00 AM Break

From Discovery to Translation

Moderator: Katja Weinacht

11:00 - 11:25 AM

Euan Ashley, PhD, Associate Dean, Roger and Joelle Burnell Professor of Genomics and Precision Health

"Precision Diagnostics for Precision Therapeutics"

11:25 - 11:50 AM

Tushar Desai, MD, Robert A. and Gertrude T. Hudson Professor of Pulmonary, Allergy & Critical Care Medicine, ISCBRM, Stanford University

"Stem Cell Transplantation for Refractory Cystic Fibrosis Sinus Disease: Status Update and Emerging Questions"

11:50 - 12:15 PM

Tippi Mackenzie, MD, Director, The Eli and Edythe Broader Center of Regeneration Medicine and Stem Cell Research, UCSF

"Fetal Therapies for Single Gene Disorders"

12:15 - 12:40 PM

Melody Smith, MD, Assistant Professor, Division of Blood & Marrow Transplantation and Cellular Therapy, Stanford University

"Donor CAR T Cell Therapy Following Allogenic Hematopoetic Stem Cell Transplantation as a strategy to Decrease Disease Relapse"

12:40 - 1:45 PM Lunch Break/Sponsor Presentations

Translational Partnerships

Moderator: Fraser Wright

1:45 - 2:10 PM

Neehar Bhatia Memorial Lecture: Mohamed Abou-el-Enein, MD, PhD, MSPH, Executive Director, USC/CHLA Cell Therapy Program

"From Concept to Reality: Establishing a Successful Cell Therapy Ecosystem at USC"

2:10 - 2:35 PM

Peter Marks, MD, PhD, Director, Center for Biologics Evaluation and Research, FDA

"FDA's Regulatory Framework for Cell and Gene Therapies"

2:35 - 3:00 PM

Bill Lis, Chairman, Jasper Therapeutics Inc; Director, Zai Laboratories Inc; Operating Executive, Abingworth Ventures

"Academic - Industry Collaboration: A Lifeblood of Therapeutic Innovation"

3:00 - 3:30 PM Break

Gene-Corrected Sickle Cell Therapy Panel

Moderator: Natalia Gomez-Ospina

3:30 - 4:45 PM Matthew Porteus, MD, PhD, Director, CDCM, Stanford University
David Shyr, MD, Clinical Assistant Professor of Pediatrics, Stem Cell Transplantation, Stanford University
Jerry Cacia, CTO, Graphite Bio
Zariah Stevenson (Patient Perspective)
Closing Remarks
5:00 PM Networking with Wine & Cheese

We look forward to welcoming everyone back to an in-person and virtual format this year. If you have any questions, please contact us at: