| Publication Title |
Publication Access |
| Enasidenib drives human erythroid differentiation independently of isocitrate dehydrogenase 2 |
Link |
| Gene correction for SCID-X1 in long-term hematopoietic stem cells |
Link |
| A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cells |
Link |
| CD34 expression does not correlate with immunophenotypic stem cell or progenitor content in human cord blood products |
Link |
| CRISPR-based gene editing enables FOXP3 gene repair in IPEX patient cells |
Link |
| Priming Human Repopulating Hematopoietic Stem and Progenitor Cells for Cas9/sgRNA Gene Targeting |
Link |
| Cas9-AAV6-engineered human mesenchymal stromal cells improved cutaneous wound healing in diabetic mice |
Link |
| Differential induction of IFN-α and modulation of CD112 and CD54 expression governs the magnitude of NK cell IFN-γ response to influenza A viruses1 |
Link |
| Multiplexed genetic engineering of human hematopoietic stem and progenitor cells using CRISPR/Cas9 and AAV6 |
|
| Identification of preexisting adaptive immunity to Cas9 proteins in humans |
Link |
| High-efficiency CRISPR induction of t(9;11) chromosomal translocations and acute leukemias in human blood stem cells |
Link |
| The TRACE-Seq method tracks recombination alleles and identifies clonal reconstitution dynamics of gene targeted human hematopoietic stem cells |
Link |
| Interferon priming is essential for human CD34+ cell-derived plasmacytoid dendritic cell maturation and function |
Link |
| CRISPR/Cas9 Beta-globin Gene Targeting in Human Hematopoietic Stem Cells |
Link |
| Engineering monocyte/macrophage−specific glucocerebrosidase expression in human hematopoietic stem cells using genome editing |
Link |
| Gene Editing Rescues in vitro T Cell Development of RAG2-Deficient Induced Pluripotent Stem Cells in an Artificial Thymic Organoid System |
Link |
| Irradiation- and busulfan-free stem cell transplantation in Fanconi anemia using an anti-CD117 antibody: a phase 1b trial |
Link |