News and events

  • – The Stem Cellar

    Joining the movement to fight rare diseases

    Today, February 28th, is Rare Disease Day. It’s a day to remind ourselves of the millions of people, and their families, struggling with these diseases. These conditions are also called or orphan diseases because, in many cases, drug companies were not interested in adopting them to develop treatments. At the California Institute for Regenerative Medicine (CIRM), we have no such reservations. In fact last Friday our governing Board voted to invest almost $12 million to support a clinical trial for IPEX syndrome.

  • – The Stem Cellar

    Stem Cell Agency Board Approves Funding for Rare Immune Disorder

    Dr. Bacchetta has received approval from the Food and Drug Administration (FDA) to test this approach in a Phase 1 clinical trial for patients suffering with IPEX syndrome.

  • – Stanford Medicine

    Young brothers with IPEX syndrome beat transplant odds

    Two young brothers beat the odds against successful stem cell transplants to halt the symptoms of a rare genetic disease called IPEX syndrome.

  • – Eventbrite

    4th Annual Center for Definitive and Curative Medicine Symposium

    Learn about new cell, gene, and regenerative medicine discoveries, pre-clinical development and clinical trials of curative medicines and challenges in bringing these cures to market at this one-day conference for clinicians, basic scientists, patient advocates, translational investigators and biotech and pharmaceutical experts.

  • – The Stem Cellar

    What is IPEX syndrome? A deeper dive into a CIRM funded award

    Brian Lookofsky (left) and his son Taylor Lookofsky (right) at the CIRM Board meeting on October 31, 2019. Taylor is living with IPEX syndrome. Last week we shared a powerful story of patient advoc…

Feb February 27 Tue 2018

2nd Annual Center for Definitive and Curative Medicine (CDCM) Symposium – Innovations in the Pipeline to Curative Medicines

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Feb February 03 Fri 2017

1st Annual Center for Definitive and Curative Medicine (CDCM) Symposium – Curing the Uncurable through Definitive Medicine

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Mar March 11 Fri 2016

Alex's Lemonade Stand Foundation Announces New Reach Grant Recipients


Dec December 2015

Notable People 2015


Jan January 2015

Alex's Lemonade Stand funded "Adoptive Immunotherapy of Tr1 Cells to Improve Outcome of Allo-HSCT Treatment for Pediatric AML" 


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