Clinical Trials
We are very interested in the clinical translation of our work and have been pursuing clinical studies.
Open clinical studies originating from our work:
- RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A
- Phase II: RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A
- AMG191* Conditioning/CD34+CD90+ Stem Cell Transplant Study for SCID Patients. (*Renamed JSP191)
- JSP191 Antibody Conditioning Regimen in MDS/AML Subjects Undergoing Allogenic Hematopoietic Stem Cell Transplantation
- JSP191 Conditioning and TCRαβ+ T-cell/CD19+ B-cell Depleted Graft for Fanconi Anemia Patients