Clinical Trials

We are very interested in the clinical translation of our work and have been pursuing clinical studies.

 

Open clinical studies originating from our work:

  • RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A
  • Phase II: RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A
  • AMG191* Conditioning/CD34+CD90+ Stem Cell Transplant Study for SCID Patients. (*Renamed JSP191)
  • JSP191 Antibody Conditioning Regimen in MDS/AML Subjects Undergoing Allogenic Hematopoietic Stem Cell Transplantation
  • JSP191 Conditioning and TCRαβ+ T-cell/CD19+ B-cell Depleted Graft for Fanconi Anemia Patients 

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